News

January 8, 2021January 8, 2021

RHB-204, Oral Treatment for MAC Lung Infections, Put on FDA Fast Track

News

The U.S. Food and Drug Administration (FDA) has given fast track designation to RedHill Biopharma’s RHB-204 as a potential first-line and stand-alone, oral treatment for lung infections caused by Mycobacterium ... Read more

January 4, 2021January 4, 2021

Corticosteroid Use Higher in Children With Bronchiectasis Who Have Asthma

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Children with non-cystic fibrosis (CF) bronchiectasis are more likely be prescribed inhaled corticosteroids — medications normally used to treat asthma — to manage their disease when they have certain asthma-like ... Read more

December 21, 2020December 21, 2020

Hypertonic Saline May Boost Benefits of Airway Clearance Techniques in Children

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Airway clearance techniques (ACTs) incorporating the use of hypertonic saline solutions — solutions with a higher salt concentration than blood plasma — for nebulization can improve lung function and lower ... Read more

December 18, 2020December 18, 2020

Endothelial Progenitor Cells (EPCs) Linked to Disease Severity in Study

News

People with bronchiectasis have lower-than-normal numbers of endothelial progenitor cells (EPCs) in their blood, a study suggests. The results indicate a link between low EPC activity and greater disease severity. ... Read more

December 14, 2020December 14, 2020

Young Bronchiectasis Patients Less Prepared to Shift to Adult Healthcare, NZ Study Finds

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Young patients with non-CF bronchiectasis are less prepared than those with cystic fibrosis (CF) to transition from pediatric to adult healthcare services, a study in New Zealand has found. This ... Read more

December 11, 2020December 11, 2020

Savara Discontinues Apulmiq Program for NCFB Amid Cost-cutting Measures

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Savara Pharmaceuticals has discontinued its clinical program of the inhaled antibiotic formulation Apulmiq (ciprofloxacin) for the treatment of non-cystic fibrosis bronchiectasis (NCFB). This decision comes with the announcement of Savara‘s ... Read more

December 7, 2020December 7, 2020

Study Recommends Longer Rest Interval Between 6-min Walk Tests for Non-CF Bronchiectasis Patients

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Two consecutive six-minute walk tests (6MWT) — which measure the distance a patient can walk in that time to assess their exercise capacity — with the recommended rest interval of ... Read more

December 4, 2020December 4, 2020

Phase 3 ASPEN Trial Testing Brensocatib Now Recruiting; First Patient Dosed

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The first participant has been dosed in ASPEN, a Phase 3 trial — now recruiting patients — that is evaluating the investigational medication brensocatib in people with non-cystic fibrosis (CF) ... Read more

December 3, 2020December 3, 2020

NORD Push for Rare Disease Advisory Councils Focus of Dec. 16 Public Meeting

News, syndicated

To empower and equip members of the rare disease community to engage state leaders in matters of importance to patients and their families, the National Organization for Rare Disorders (NORD) ... Read more

November 26, 2020November 26, 2020

Survey Finds COVID-19 Disrupted Care, Well-Being of Rare Disease Patients in Europe

News, syndicated

The first wave of COVID-19 in Europe severely disrupted access to care and raised stress and anxiety in people with rare diseases, negatively affecting their health and well-being, according to a ... Read more