Updates

December 4, 2020December 4, 2020
Phase 3 ASPEN Trial Testing Brensocatib Now Recruiting; First Patient Dosed

The first participant has been dosed in ASPEN, a Phase 3 trial — now recruiting patients — that is evaluating the investigational medication brensocatib ... Read more
December 3, 2020December 3, 2020
NORD Push for Rare Disease Advisory Councils Focus of Dec. 16 Public Meeting

To empower and equip members of the rare disease community to engage state leaders in matters of importance to patients and their families, the ... Read more
November 26, 2020November 26, 2020
Survey Finds COVID-19 Disrupted Care, Well-Being of Rare Disease Patients in Europe

The first wave of COVID-19 in Europe severely disrupted access to care and raised stress and anxiety in people with rare diseases, negatively affecting their ... Read more
November 23, 2020November 23, 2020
RedHill Launches Trial to Test RHB-204 for Bronchiectasis Plus MAC Lung Infections

RedHill Biopharma has launched a Phase 3 clinical trial to evaluate the safety and effectiveness of its investigational oral therapy RHB-204 in adults with ... Read more
November 20, 2020November 20, 2020
Latest NORD Webinar Offers Insights on Starting Nonprofit, Patient Registry

Leaders in the U.S. rare disease community came together recently for a webinar to present helpful information on how to start a nonprofit and ... Read more

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April 10, 2017

What a Doctor Wants People to Know About Chronic Illnesses

Social Clips

Having a chronic illness presents many challenges for patients, not only in terms of managing the symptoms they suffer but also having to deal with people’s preconceived ideas about invisible illnesses. MORE: What to expect when living with bronchiectasis. Dr. ... Read more

Phase 3 ASPEN Trial Testing Brensocatib Now Recruiting; First Patient Dosed

NORD Push for Rare Disease Advisory Councils Focus of Dec. 16 Public Meeting

Survey Finds COVID-19 Disrupted Care, Well-Being of Rare Disease Patients in Europe

RedHill Launches Trial to Test RHB-204 for Bronchiectasis Plus MAC Lung Infections

Latest NORD Webinar Offers Insights on Starting Nonprofit, Patient Registry

EMA Grants PRIME Status to Brensocatib for Treating Non-CF Bronchiectasis

Bronchiectasis Worsens Lung Function, Quality of Life in Severe Asthma, Study Finds

Being Underweight Linked to Poorer Lung Function in Bronchiectasis Patients in US Study

NORD Hosting ‘RareLaunch’ Workshops to Help Start Rare Disease Non-profits

South Korean Tuberculosis Control Program May Have Contributed to Lower Bronchiectasis Rates

Arikayce Approved in Europe for MAC Lung Infections in Non-CF Adults

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UK Organization ‘Same But Different’ Announces ‘Glimmer of Hope’ Photo Contest Winner

Bronchiectasis Increases Mortality Risk in People With Steroid-dependent Severe Asthma, Study Finds

Telehealth ‘Helpful’ Alternative to In-person Care, Rare Disease Patients Say

Bronchiectasis Could Be Diagnosis for Children With Persistent Wet Cough, Case Report Says

Sit-to-stand Test Ably Captures Exercise Capacity of Children, Study Finds

Symptoms of Flares Distinct for Viruses and Bacteria, Study Finds

Patients With Bronchiectasis Linked to Tuberculosis May Develop More Severe Disease

Same But Different Asks Public to Vote on ‘Glimmer of Hope’ Calendar Photos

Phase 3 Trial Testing Brensocatib for Bronchiectasis Set to Start Soon

Mild, Severe Bronchiectasis Linked to Different Airway Bacteria, Study Finds

Immune Cells Ratio May Be Used as Biomarker of Exacerbations, Study Reports

Disease Duration, Flare-ups Affect Mental Health of Non-CF Bronchiectasis Patients, Study Finds

E-cigarette Use Linked to Bronchiectasis in 3 Cases, Report Suggests

Brensocatib Significantly Lowers Flare Risk in Non-CF Bronchiectasis, Trial Shows

Bronchiectasis Aggravates Asthma Outcomes, Review Study Finds

Case Study Reports COVID-19 Plus Rare Bacterial Infection in Bronchiectasis Patient

Same But Different Photo Contest Celebrates People With Rare Diseases

Analysis Links Pneumonia With Bronchiectasis to Less Mortality, More Infections

Protein May Help Monitor Inflammation During, After Bronchiectasis Exacerbations

Xperiome Platform Aims to Streamline Searches for Rare Diseases, Gain Patient Input

Inflammatory Biomarkers Linked to More Severe Disease in COPD With Bronchiectasis

Dry Powder Inhaled Antibiotics Safe, Effective for Bronchiectasis, Study Suggests

EveryLife Foundation Launches Scholarship Fund for Rare Disease Community in US

Use of Airway Clearance Techniques Rises With Flares and Infections

New Streaming Channel Showcases Rare Disease Films

Vest Therapy Lowers Risk of Hospitalization in Non-CF Bronchiectasis, Study Says

CHMP Recommends Arikayce for MAC Lung Infections in Europe

Rare Disease Communities Invited to Submit Works to 2020 Rare Artist Contest